Treatment of severe combined immunodeficiency disease (SCID) due to adenosine deaminase deficiency with autologous lymphocytes transduced with a human ADA gene

R. M. Blaese, K. Culver, W. F. Anderson, A. Nienhuis, C. Dunbar, L. Chang, C. Mullen, C. Carter, S. Leitman, M. Berger, A. D. Miller, R. Morgan, T. Fleisher, R. Kobyashi, A. L. Kobyashi, H. Klein, G. Shearer, M. Clerici, G. McGarrity, A. Cassell

Research output: Contribution to journalArticlepeer-review

86 Scopus citations
Original languageEnglish
Pages (from-to)521-527
Number of pages7
JournalHuman Gene Therapy
Volume4
Issue number4
StatePublished - Aug 1993

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