Therapeutic goals in Fabry disease: Recommendations of a European expert panel, based on current clinical evidence with enzyme replacement therapy

Christoph Wanner, Dominique P. Germain, Max J. Hilz, Marco Spada, Bruno Falissard, Perry M. Elliott

Research output: Contribution to journalComment/debate

15 Scopus citations
Original languageEnglish
Pages (from-to)210-211
Number of pages2
JournalMolecular Genetics and Metabolism
Volume126
Issue number3
DOIs
StatePublished - Mar 2019
Externally publishedYes

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