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Safety and efficacy of 22 weeks of treatment with sapropterin dihydrochloride in patients with phenylketonuria

  • Phillip Lee
  • , Eileen P. Treacy
  • , Eric Crombez
  • , Melissa Wasserstein
  • , Lewis Waber
  • , Jon Wolff
  • , Udo Wendel
  • , Alex Dorenbaum
  • , Judith Bebchuk
  • , Heidi Christ-Schmidt
  • , Margretta Seashore
  • , Marcello Giovannini
  • , Barbara K. Burton
  • , Andrew A. Morris

Research output: Contribution to journalArticlepeer-review

85 Scopus citations

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Biochemistry, Genetics and Molecular Biology

Pharmacology, Toxicology and Pharmaceutical Science