Production and characterization of vectors based on the cardiotropic AAV serotype 9

Erik Kohlbrenner, Thomas Weber

Research output: Chapter in Book/Report/Conference proceedingChapterpeer-review

17 Scopus citations

Abstract

Vectors based on adeno-associated virus serotype 9 (AAV9) efficiently transduce cardiomyocytes in both rodents and large animal models upon either systemic or regional vector delivery. In this chapter, we describe the most widely used production and purification method of AAV9. This production approach does not depend on the use of a helpervirus but instead on transient transfection of HEK293T cells with a plasmid containing the recombinant AAV genome and a second plasmid encoding the AAV9 capsid proteins, the AAV Rep proteins and the adenoviral helper functions. The recombinant AAV is then purified by iodixanol density gradient centrifugation. This chapter also describes in detail the characterization and quality control methods required for assuring high quality vector preparations, which is of particular importance for experiments in large animal models.

Original languageEnglish
Title of host publicationMethods in Molecular Biology
PublisherHumana Press Inc.
Pages91-107
Number of pages17
DOIs
StatePublished - 2017

Publication series

NameMethods in Molecular Biology
Volume1521
ISSN (Print)1064-3745

Keywords

  • AAV
  • AAV characterization
  • AAV production
  • AAV9
  • Adeno-associated virus
  • Cardiotropic
  • Gene therapy
  • Serotype

Fingerprint

Dive into the research topics of 'Production and characterization of vectors based on the cardiotropic AAV serotype 9'. Together they form a unique fingerprint.

Cite this